Items where Author is "Wall, D."
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Article
Frangoul, H. and Locatelli, F. and Sharma, A. and Bhatia, M. and Mapara, M. and Molinari, L. and Wall, D. and Liem, R. I. and Telfer, P. and Shah, A. J. and Cavazzana, M. and Corbacioglu, Selim and Rondelli, D. and Meisel, R. and Dedeken, L. and Lobitz, S. and de Montalembert, M. and Steinberg, M. H. and Walters, M. C. and Eckrich, M. J. and Imren, S. and Bower, L. and Simard, C. and Zhou, W. and Xuan, F. and Morrow, P. K. and Hobbs, W. E. and Grupp, S. A. (2024) Exagamglogene Autotemcel for Severe Sickle Cell Disease. NEW ENGLAND JOURNAL OF MEDICINE, 390 (18). pp. 1649-1662. ISSN 0028-4793, 1533-4406
Locatelli, F. and Lang, P. and Wall, D. and Meisel, R. and Corbacioglu, Selim and Li, A. M. and de la Fuente, J. and Shah, A. J. and Carpenter, B. and Kwiatkowski, J. L. and Mapara, M. and Liem, R. I. and Cappellini, M. D. and Algeri, M. and Kattamis, A. and Sheth, S. and Grupp, S. and Handgretinger, R. and Kohli, P. and Shi, D. and Ross, L. and Bobruff, Y. and Simard, C. and Zhang, L. and Morrow, P. K. and Hobbs, W. E. and Frangoul, H. (2024) Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia. NEW ENGLAND JOURNAL OF MEDICINE, 390 (18). pp. 1663-1676. ISSN 0028-4793, 1533-4406
Frangoul, H. and Altshuler, D. and Cappellini, M. D. and Chen, Y-S and Domm, J. and Eustace, B. K. and Foell, J. and de la Fuente, J. and Grupp, S. and Handgretinger, R. and Ho, T. W. and Kattamis, A. and Kernytsky, A. and Lekstrom-Himes, J. and Li, A. M. and Locatelli, F. and Mapara, M. Y. and de Montalembert, M. and Rondelli, D. and Sharma, A. and Sheth, S. and Soni, S. and Steinberg, M. H. and Wall, D. and Yen, A. and Corbacioglu, S. (2021) CRISPR-Cas9 Gene Editing for Sickle Cell Disease and beta-Thalassemia. NEW ENGLAND JOURNAL OF MEDICINE, 384 (3). pp. 252-260. ISSN 0028-4793, 1533-4406
Gerbens, L. A. A. and Apfelbacher, C. J. and Irvine, A. D. and Barbarot, S. and de Booij, R. J. and Boyce, A. E. and Deleuran, M. and Eichenfield, L. F. and Hof, M. H. and Middelkamp-Hup, M. A. and Roberts, A. and Schmitt, J. and Vestergaard, C. and Wall, D. and Weidinger, S. and Williamson, P. R. and Flohr, C. and Spuls, P. I. (2019) TREatment of ATopic eczema (TREAT) Registry Taskforce: an international Delphi exercise to identify a core set of domains and domain items for national atopic eczema photo- and systemic therapy registries. BRITISH JOURNAL OF DERMATOLOGY, 180 (4). pp. 790-801. ISSN 0007-0963, 1365-2133
Vermeulen, F. M. and Gerbens, L. A. A. and Bosma, A. L. and Apfelbacher, C. J. and Irvine, A. D. and Arents, B. W. M. and Barbarot, S. and Deleuran, M. and Eichenfield, L. F. and Manca, A. and Schmitt, J. and Vestergaard, C. and Wall, D. and Weidinger, S. and Middelkamp-Hup, M. A. and Spuls, P. I. and Flohr, C. (2019) TREatment of ATopic eczema (TREAT) Registry Taskforce: consensus on how and when to measure the core dataset for atopic eczema treatment research registries. BRITISH JOURNAL OF DERMATOLOGY, 181 (3). pp. 492-504. ISSN 0007-0963, 1365-2133
Conference or Workshop Item
Meisel, R. and Frangoul, H. and Locatelli, F. and Sharma, A. and Bhatia, M. and Molinari, L. and Wall, D. and Liem, R. and Telfer, P. and Shah, A. and Cavazzana, M. and Corbacioglu, S. and Rondelli, D. and Dedeken, L. and Lobitz, S. and de Montalembert, M. and Steinberg, M. and Walters, M. and Imren, S. and Shi, D. and Bower, L. and Simard, C. and Zhang, L. and Morrow, P. K. and Hobbs, B. and Grupp, S. (2023) Elimination of vaso-occlusive crises after exagamglogene autotemcel in patients with severe Sickle Cell Disease. In: Jahrestagung der Deutschen, Österreichischen und Schweizerischen Gesellschaften für Hämatologie und Medizinische Onkologie, 13. bis 16. Oktober 2023, Hamburg, Germany.
Corbacioglu, S. and Locatelli, F. and Lang, P. and Li, A. and De La Fuente, J. and Wall, D. and Meisel, R. and Shah, A. and Liem, R. and Mapara, M. and Carpenter, B. and Kwiatkowski, J. and Cappellini, M. and Kattamis, A. and Sheth, S. and Grupp, S. and Kohli, P. and Shi, D. and Bobruff, Y. and Ross, L. and Simard, C. and Zhang, L. and Morrow, P. K. and Hobbs, B. and Frangoul, H. (2023) Transfusion independence after exagamglogene autotemcel in patients with transfusion-dependent β-thalassemia. In: Jahrestagung der Deutschen, Österreichischen und Schweizerischen Gesellschaften für Hämatologie und Medizinische Onkologie, 13. bis 16. Oktober 2023, Hamburg, Germany.
Locatelli, F. and Ailinca-Luchian, S. and Bobruff, Y. and Cappellini, M. Domenica and Corbacioglu, Selim and Domm, J. and Foell, J. and De la Fuente, J. and Handgretinger, R. and Ho, T. W. and Hobbs, W. and Kattamis, A. and Li, A. and Lu, Y. and Palomino, L. and Shanbhag, N. and Sharma, A. and Sheth, S. and Sripakdeevong, P. and Wall, D. and Frangoul, H. (2021) CTX001 FOR TRANSFUSION-DEPENDENT -THALASSEMIA (TDT): SAFETY AND EFFICACY RESULTS FROM THE ONGOING CLIMB THAL-111 STUDY OF AUTOLOGOUS CRISPR-CAS9-MODIFIED CD34+HEMATOPOIETIC STEM AND PROGENITOR CELLS (HSPCS). In: 48th Congress of the Italian Society of Hematology, 24 - 27 October 2021, Milano, Italy.
Corbacioglu, Selim and Locatelli, F. and Ailinca-Luchian, S. and Bobruff, Y. and Cappellini, M. D. and Domm, J. and Foell, J. and de la Fuente, J. and Handgretinger, R. and Ho, T. W. and Hobbs, W. and Kattamis, A. and Li, A. and Lu, Y. and Palomino, L. and Shanbhag, N. and Sharma, A. and Sheth, S. and Sripakdeevong, P. and Wall, D. and Frangoul, H. (2021) CTX001 for transfusion-dependent beta-thalassemia (TDT): safety and efficacy results from the ongoing CLIMB THAL-111 study of autologous CRISPR-CAS9-modified CD34(+) hematopoietic stem and progenitor cells (HSPCs). In: Jahrestagung der Deutschen, Österreichischen und Schweizerischen Gesellschaften für Hämatologie und Medizinische Onkologie, 01.-04. Oktober 2021, Berlin, Germany.
Ho, T. W. and Frangoul, H. and Bobruff, Y. and Cappellini, M. D. and Corbacioglu, Selim and Fernandez, C. M. and de la Fuente, J. and Grupp, S. and Handgretinger, R. and Imren, S. and Kattamis, A. and Lekstrom-Himes, J. and Locatelli, F. and Lu, Y. and Mapara, M. and Mulcahey, S. and de Montalembert, M. and Rondelli, D. and Shanbhag, N. and Sheth, S. and Soni, S. and Steinberg, M. H. and Weinstein, M. and Wu, J. and Wall, D. (2021) Safety and Efficacy Results with a Single Dose of Autologous CRISPR-Cas9-Modified CD34(+) Hematopoietic Stem and Progenitor Cells (HSPCs) in Transfusion-Dependent beta-Thalassemia (TDT) and Sickle Cell Disease (SCD). In: 24th Annual Meeting of the American Society of Gene & Cell Therapy, May 11 - 14, 2021, Virtual.
Other
Bosma, A. L. and Spuls, P. I. and Garcia-Doval, I. and Naldi, L. and Prieto-Merino, D. and Tesch, F. and Apfelbacher, C. J. and Arents, B. W. M. and Barbarot, S. and Baselga, E. and Deleuran, M. and Eichenfield, L. F. and Gerbens, L. A. A. and Irvine, A. D. and Manca, A. and Mendes-Bastos, P. and Middelkamp-Hup, M. A. and Roberts, A. and Seneschal, J. and Svensson, A. and Thyssen, J. P. and Torres, T. and Vermeulen, F. M. and Vestergaard, C. and von Kobyletzki, L. B. and Wall, D. and Weidinger, S. and Schmitt, J. and Flohr, C. (2019) TREatment of ATopic eczema (TREAT) Registry Taskforce: protocol for a European safety study of dupilumab and other systemic therapies in patients with atopic eczema. WILEY, HOBOKEN.
Gerbens, L. A. A. and Vermeulen, F. M. and Apfelbacher, C. J. and Irvine, A. D. and Arents, B. W. M. and Barbarot, S. and De Booij, R. J. and Bosma, A. L. and Deleuran, M. and Eichenfield, L. F. and Hof, M. H. and Middelkamp-Hup, M. A. and Roberts, A. and Schmitt, J. and Vestergaard, C. and Wall, D. and Weidinger, S. and Williamson, P. R. and Flohr, C. and Spuls, P. I. (2018) Treatment of Atopic Dermatitis (TREAT) Registry Taskforce: an international exercise to harmonize data collection for national atopic eczema registries. WILEY, HOBOKEN.

