Items where Division is "Medicine > Abteilung für Pädiatrische Hämatologie, Onkologie und Stammzelltransplantation" and Year is 2024

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Aldebert, Clemence and Fahd, Mony and Galimard, Jacques-Emmanuel and Ghemlas, Ibrahim A. and Zecca, Marco and Silva, Juliana and Mohseny, Alexander and Kupesiz, Alphan and Hamladji, Rose-Marie and Miranda, Nuno and Gungor, Tayfun and Wynn, Robert F. and Merli, Pietro and Sundin, Mikael and Faraci, Maura and Diaz-de-Heredia, Cristina and Burkhardt, Birgit and Bordon, Victoria and Angoso, Marie and Bader, Peter and Ifversen, Marianne and Herrera Arroyo, Concepcion and Maximova, Natalia and Riesco, Susana and Stein, Jerry and Dalissier, Arnaud and Locatelli, Franco and Kalwak, Krzysztof and Dalle, Jean-Hugues and Corbacioglu, Selim (2024) Outcomes of patients undergoing allogeneic haematopoietic stem cell transplantation for congenital amegakaryocytic thrombocytopenia; a study on behalf of the PDWP of the EBMT. BONE MARROW TRANSPLANTATION, 59 (12). pp. 1717-1725. ISSN 0268-3369, 1476-5365

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Corbacioglu, Selim and Frangoul, Haydar and Locatelli, Franco and Hobbs, William and Walters, Mark (2024) Defining curative endpoints for transfusion-dependent β-thalassemia in the era of gene therapy and gene editing. AMERICAN JOURNAL OF HEMATOLOGY, 99 (3). pp. 422-429. ISSN 0361-8609, 1096-8652

Corbacioglu, Selim and Lode, Holger and Ellinger, Susanne and Zeman, Florian and Suttorp, Meinolf and Escherich, Gabriele and Bochennek, Konrad and Gruhn, Bernd and Lang, Peter and Rohde, Marius and Debatin, Klaus Michael and Steinbach, Daniel and Beilken, Andreas and Ladenstein, Ruth and Spachtholz, Rainer and Heiss, Peter and Hellwig, Dirk and Troeger, Anja and Koller, Michael and Menhart, Karin and Riemenschneider, Markus J. and Zoubaa, Saida and Kietz, Silke and Jakob, Marcus and Sommer, Gunhild and Heise, Tilman and Hundsdoerfer, Patrick and Kuehnle, Ingrid and Dilloo, Dagmar and Schoenberger, Stefan and Schwabe, Georg and von Luettichau, Irene and Graf, Norbert and Schlegel, Paul-Gerhardt and Fruehwald, Michael and Jorch, Norbert and Paulussen, Michael and Schneider, Dominik T. and Metzler, Markus and Leipold, Alfred and Nathrath, Michaela and Imschweiler, Thomas and Christiansen, Holger and Schmid, Irene and Crazzolara, Roman and Niktoreh, Naghmeh and Cario, Gunnar and Faber, Joerg and Demmert, Martin and Babor, Florian and Froehlich, Birgit and Bielack, Stefan and Bernig, Toralf and Greil, Johann and Eggert, Angelika and Simon, Thorsten and Foell, Juergen (2024) Irinotecan and temozolomide in combination with dasatinib and rapamycin versus irinotecan and temozolomide for patients with relapsed or refractory neuroblastoma (RIST-rNB-2011): a multicentre, open-label, randomised, controlled, phase 2 trial. LANCET ONCOLOGY, 25 (7). pp. 922-932. ISSN 1470-2045, 1474-5488

Cseh, Annamaria and Galimard, Jacques-Emmanuel and de la Fuente, Josu and Isgro, Antonella and Zecca, Marco and Garwer, Birgit and Biffi, Alexandra and Aljurf, Mahmoud and Sundin, Mikael and Belendez, Cristina and Locatelli, Franco and Balduzzi, Adriana and Lawson, Sarah and Sengeloev, Henrik and Ifversen, Marianne and Saccardi, Riccardo and Wynn, Robert and Lankester, Arjan C. and Corbacioglu, Selim and Peters, Christina (2024) Busulfan-fludarabine- or treosulfan-fludarabine-based conditioning before allogeneic HSCT from matched sibling donors in paediatric patients with sickle cell disease: A study on behalf of the EBMT Paediatric Diseases and Inborn Errors Working Parties. BRITISH JOURNAL OF HAEMATOLOGY, 204 (1). e1-e5. ISSN 0007-1048, 1365-2141

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Feuchtinger, Tobias and Bader, Peter and Subklewe, Marion and Breidenbach, Maike and Willier, Semjon and Metzler, Markus and Goekbuget, Nicola and Hauer, Julia and Mueller, Fabian and Schlegel, Paul-Gerhardt and Fruehwald, Michael and Schmid, Christoph and Troeger, Anja and Baldus, Claudia and Meisel, Roland and Kuenkele, Annette and Topp, Max and Bourquin, Jean-Pierre and Cario, Gunnar and von Stackelberg, Arend and Peters, Christina (2024) Approaches for bridging therapy prior to chimeric antigen receptor T cells for relapsed/refractory acute lymphoblastic B-lineage leukemia in children and young adults. HAEMATOLOGICA, 109 (12). pp. 3892-3903. ISSN 0390-6078, 1592-8721

Frangoul, H. and Locatelli, F. and Sharma, A. and Bhatia, M. and Mapara, M. and Molinari, L. and Wall, D. and Liem, R. I. and Telfer, P. and Shah, A. J. and Cavazzana, M. and Corbacioglu, Selim and Rondelli, D. and Meisel, R. and Dedeken, L. and Lobitz, S. and de Montalembert, M. and Steinberg, M. H. and Walters, M. C. and Eckrich, M. J. and Imren, S. and Bower, L. and Simard, C. and Zhou, W. and Xuan, F. and Morrow, P. K. and Hobbs, W. E. and Grupp, S. A. (2024) Exagamglogene Autotemcel for Severe Sickle Cell Disease. NEW ENGLAND JOURNAL OF MEDICINE, 390 (18). pp. 1649-1662. ISSN 0028-4793, 1533-4406

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Giardino, Stefano and Eikema, Dirk-Jan and Piepenbroek, Brian and Algeri, Mattia and Ayas, Mouhab and Faraci, Maura and Tbakhi, Abdelghani and Zecca, Marco and Essa, Mohammed and Neven, Benedicte and Bertrand, Yves and Kharya, Gaurav and Bykova, Tatiana and Lawson, Sarah and Petrini, Mario and Mohseny, Alexander and Rialland, Fanny and James, Beki and Colita, Anca and Fahd, Mony and Cesaro, Simone and Schulz, Ansgar and Kleinschmidt, Katharina and Kalwak, Krzysztof and Corbacioglu, Selim and Dufour, Carlo and Risitano, Antonio and de Latour, Regis Peffault (2024) HLA-haploidentical stem cell transplantation in children with inherited bone marrow failure syndromes: A retrospective analysis on behalf of EBMT severe aplastic Anemia and pediatric diseases working parties. CURRENT SCIENCE, 126 (8). ISSN 0011-3891,

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Haegele, Pauline and Staus, Paulina and Scheible, Raphael and Uhlmann, Annette and Heeg, Maximilian and Klemann, Christian and Maccari, Maria Elena and Ritterbusch, Henrike and Armstrong, Martin and Cutcutache, Ioana and Elliott, Katherine S. and von Bernuth, Horst and Leahy, Timothy Ronan and Leyh, Joerg and Holzinger, Dirk and Lehmberg, Kai and Svec, Peter and Masjosthusmann, Katja and Hambleton, Sophie and Jakob, Marcus and Sparber-Sauer, Monika and Kager, Leo and Puzik, Alexander and Wolkewitz, Martin and Lorenz, Myriam Ricarda and Schwarz, Klaus and Speckmann, Carsten and Rensing-Ehl, Anne and Ehl, Stephan (2024) Diagnostic evaluation of paediatric autoimmune lymphoproliferative immunodeficiencies (ALPID): a prospective cohort study. LANCET HAEMATOLOGY, 11 (2). e114-e126. ISSN 2352-3026,

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Locatelli, F. and Lang, P. and Wall, D. and Meisel, R. and Corbacioglu, Selim and Li, A. M. and de la Fuente, J. and Shah, A. J. and Carpenter, B. and Kwiatkowski, J. L. and Mapara, M. and Liem, R. I. and Cappellini, M. D. and Algeri, M. and Kattamis, A. and Sheth, S. and Grupp, S. and Handgretinger, R. and Kohli, P. and Shi, D. and Ross, L. and Bobruff, Y. and Simard, C. and Zhang, L. and Morrow, P. K. and Hobbs, W. E. and Frangoul, H. (2024) Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia. NEW ENGLAND JOURNAL OF MEDICINE, 390 (18). pp. 1663-1676. ISSN 0028-4793, 1533-4406

Locatelli, Franco and Corbacioglu, Selim and Hobbs, William and Frangoul, Haydar and Walters, Mark C. (2024) Defining curative endpoints for sickle cell disease in the era of gene therapy and gene editing. AMERICAN JOURNAL OF HEMATOLOGY, 99 (3). pp. 430-438. ISSN 0361-8609, 1096-8652

Lum, Su Han and Eikema, Dirk-Jan and Piepenbroek, Brian and Wynn, Robert F. and Samarasinghe, Sujith and Dalissier, Arnaud and Kalwak, Krysztof and Ayas, Mouhab and Hamladji, Rose-Marie and Yesilipek, Akif and Dalle, Jean-Hugues and Uckan-Cetinkaya, Duygu and Bierings, Marc and Kupesiz, Alphan and Halahleh, Khalid and Skorobogatova, Elena and Ozturk, Gulyuz and Faraci, Maura and Renard, Cecile and Evans, Pamela and Corbacioglu, Selim and Locatelli, Franco and Dufour, Carlo and Risitano, Antonio and de Latour, Regis Peffault (2024) Outcomes of hematopoietic stem cell transplantation in 813 pediatric patients with Fanconi anemia. BLOOD, 144 (12). pp. 1329-1342. ISSN 0006-4971, 1528-0020

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Meissner, Barbara and Lang, Peter and Bader, Peter and Hoenig, Manfred and Mueller, Ingo and Meisel, Roland and Greil, Johann and Sauer, Martin G. and Metzler, Markus and Corbacioglu, Selim and Burkhardt, Birgit and Woelfl, Matthias and Strahm, Brigitte and Kafa, Kinan and Basu, Oliver and Lode, Holger N. and Gruhn, Bernd and Cario, Holger and Ozga, Ann-Kathrin and Zimmermann, Martin and Jarisch, Andrea and Beier, Rita (2024) Finding a balance in reduced toxicity hematopoietic stem cell transplantation for thalassemia: role of infused CD3+cell count and immunosuppression. BONE MARROW TRANSPLANTATION, 59 (5). pp. 587-596. ISSN 0268-3369, 1476-5365

Min, Kyung-Won and Choi, Kyoung-Min and Mun, Hyejin and Ko, Seungbeom and Lee, Ji Won and Sagum, Cari A. and Bedford, Mark T. and Kim, Young-Kook and Delaney, Joe R. and Cho, Jung-Hyun and Dawson, Ted M. and Dawson, Valina L. and Twal, Waleed and Kim, Dong-Chan and Panganiban, Clarisse H. and Lang, Hainan and Zhou, Xin and Shin, Seula and Hu, Jian and Heise, Tilman and Kwon, Sang-Ho and Kim, Dongsan and Kim, Young Hwa and Kang, Sung-Ung and Kim, Kyungmin and Lewis, Sydney and Eroglu, Ahmet and Ryu, Seonghyun and Kim, Dongin and Chang, Jeong Ho and Jung, Junyang and Yoon, Je-Hyun (2024) Mature microRNA-binding protein QKI suppresses extracellular microRNA let-7b release. JOURNAL OF CELL SCIENCE, 137 (21): jcs261575. ISSN 0021-9533, 1477-9137

Moser, Olga and Ngoya, Maud and Galimard, Jacques-Emmanuel and Dalissier, Arnaud and Dalle, Jean Hugues and Kalwak, Krzysztof and Woessmann, Wilhelm and Burkhardt, Birgit and Bierings, Marc and Gonzalez-Vicent, Marta and Corral, Lucia Lopez and Mellgren, Karin and Attarbaschi, Andishe and Bourhis, Jean Henri and Carlson, Kristina and Corbacioglu, Selim and Drabko, Katarzyna and Sundin, Mikael and Toporski, Jacek and Cario, Gunnar and Kontny, Udo (2024) Hematopoietic stem cell transplantation for pediatric patients with non-anaplastic peripheral T-cell lymphoma. An EBMT pediatric diseases working party study. BONE MARROW TRANSPLANTATION, 59 (5). pp. 604-614. ISSN 0268-3369, 1476-5365

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Nussbaumer, Gunther and Benesch, Martin and Grabovska, Yura and Mackay, Alan and Castel, David and Grill, Jacques and Alonso, Marta M. and Antonelli, Manila and Bailey, Simon and Baugh, Joshua N. and Biassoni, Veronica and Blattner-Johnson, Mirjam and Broniscer, Alberto and Carai, Andrea and Colafati, Giovanna Stefania and Colditz, Niclas and Corbacioglu, Selim and Crampsie, Shauna and Entz-Werle, Natacha and Eyrich, Matthias and Friker, Lea L. and Fruehwald, Michael C. and Garre, Maria Luisa and Gerber, Nicolas U. and Giangaspero, Felice and Gil-da-Costa, Maria J. and Graf, Norbert and Hargrave, Darren and Hauser, Peter and Herrlinger, Ulrich and Hoffmann, Marion and Hulleman, Esther and Izquierdo, Elisa and Jacobs, Sandra and Karremann, Michael and Kattamis, Antonis and Kebudi, Rejin and Kortmann, Rolf-Dieter and Kwiecien, Robert and Massimino, Maura and Mastronuzzi, Angela and Miele, Evelina and Morana, Giovanni and Noack, Claudia M. and Pentikainen, Virve and Perwein, Thomas and Pfister, Stefan M. and Pietsch, Torsten and Roka, Kleoniki and Rossi, Sabrina and Rutkowski, Stefan and Schiavello, Elisabetta and Seidel, Clemens and Sterba, Jaroslav and Sturm, Dominik and Sumerauer, David and Tacke, Anna and Temelso, Sara and Valentini, Chiara and van Vuurden, Dannis and Varlet, Pascale and van Zanten, Sophie E. M. Veldhuijzen and Vinci, Maria and von Bueren, Andre O. and Warmuth-Metz, Monika and Wesseling, Pieter and Wiese, Maria and Wolff, Johannes E. A. and Zamecnik, Josef and Morales La Madrid, Andres and Bison, Brigitte and Gielen, Gerrit H. and Jones, David T. W. and Jones, Chris and Kramm, Christof M. (2024) Gliomatosis cerebri in children: A poor prognostic phenotype of diffuse gliomas with a distinct molecular profile. NEURO-ONCOLOGY, 26 (9). pp. 1723-1737. ISSN 1522-8517, 1523-5866

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Obrecht-Sturm, Denise and Pfaff, Elke and Mynarek, Martin and Bison, Brigitte and Rodehueser, Martina and Becker, Martina and Kietz, Silke and Pfister, Stefan M. and Jones, David T. and Sturm, Dominik and von Deimling, Andreas and Sahm, Felix and Kortmann, Rolf-Dieter and Schwarz, Rudolf and Pietsch, Torsten and Fleischhack, Gudrun and Rutkowski, Stefan (2024) Pineal anlage tumor: clinical and diagnostic features, and rationales for treatment. JOURNAL OF NEURO-ONCOLOGY, 166 (2). pp. 359-368. ISSN 0167-594X, 1573-7373

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Reger, Mira and Manz, Kirsi and Kaeuferle, Theresa and Coffey, Ramona and Wotschofsky, Zofia and von Luettichau, Irene and Schlegel, Paul-Gerhardt and Fruehwald, Michael C. and Corbacioglu, Selim and Metzler, Markus and Feuchtinger, Tobias (2024) Impact of regional SARS-CoV-2 proceedings on changes in diagnoses of pediatric malignancies in Bavaria during the COVID-19 pandemic. PEDIATRIC HEMATOLOGY AND ONCOLOGY, 41 (7). pp. 504-518. ISSN 0888-0018, 1521-0669

Ruggeri, Annalisa and Santoro, Nicole and Galimard, Jacques-Emmanuel and Kalwak, Krzysztof and Algeri, Mattia and Zubarovskaya, Ludmila and Czyzewski, Krzysztof and Skorobogatova, Elena and Sedlacek, Petr and Besley, Caroline and Balduzzi, Adriana and Bertrand, Yves and Peristeri, Julia and Fagioli, Franca and Ifversen, Mariane and Gozdzik, Jolanta and Peters, Christina and Versluijs, Birgitta and Biffi, Alessandra and Prete, Arcangelo and Faraci, Maura and Ghemlas, Ibrahim and Bodova, Ivana and Aleinikova, Olga and Dalissier, Arnaud and Rocha, Vanderson and Corbacioglu, Selim (2024) Matched unrelated donor transplantation versus haploidentical transplantation with post-transplant cyclophosphamide in children with acute myeloid leukemia: a PDWP-EBMT study. HAEMATOLOGICA, 109 (7). pp. 2122-2130. ISSN 0390-6078, 1592-8721

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Sanchez-Guijo, Fermin and Vives, Joaquim and Ruggeri, Annalisa and Chabannon, Christian and Corbacioglu, Selim and Dolstra, Harry and Farge, Dominique and Gagelmann, Nico and Horgan, Claire and Kuball, Jurgen and Neven, Benedicte and Rintala, Tuula and Rocha, Vanderson and Sanchez-Ortega, Isabel and Snowden, John A. and Zwaginga, Jaap Jan and Gnecchi, Massimiliano and Sureda, Anna (2024) Current challenges in cell and gene therapy: a joint view from the European Committee of the International Society for Cell & Gene Therapy (ISCT) and the European Society for Blood and Marrow Transplantation (EBMT). CYTOTHERAPY, 26 (7). pp. 681-685. ISSN 1465-3249, 1477-2566

Sharma, Akshay and Galimard, Jacques-Emmanuel and Pryce, Angharad and Bhoopalan, Senthil Velan and Dalissier, Arnaud and Dalle, Jean-Hugues and Locatelli, Franco and Jubert, Charlotte and Mirci-Danicar, Oana and Kitra-Roussou, Vassiliki and Bertrand, Yves and Fagioli, Franca and Rialland, Fanny and Biffi, Alessandra and Wynn, Robert F. and Michel, Gerard and Tambaro, Francesco Paolo and Al-Ahmari, Ali and Tbakhi, Abdelghani and Furness, Caroline L. and Diaz, Miguel Angel and Sedlacek, Petr and Bodova, Ivana and Faraci, Maura and Rao, Kanchan and Kleinschmidt, Katharina and Petit, Arnaud and Gibson, Brenda and Bhatt, Neel S. and Kalwak, Krzysztof and Corbacioglu, Selim (2024) Cytogenetic abnormalities predict survival after allogeneic hematopoietic stem cell transplantation for pediatric acute myeloid leukemia: a PDWP/EBMT study. BONE MARROW TRANSPLANTATION, 59 (4). pp. 451-458. ISSN 0268-3369, 1476-5365

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Torkler, Phillipp and Sauer, Marina and Schwartz, Uwe and Corbacioglu, Selim and Sommer, Gunhild and Heise, Tilman (2024) LoDEI: a robust and sensitive tool to detect transcriptome-wide differential A-to-I editing in RNA-seq data. NATURE COMMUNICATIONS, 15 (1): 9121. ISSN , 2041-1723

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Wachowiak, Jacek and Galimard, Jacques-Emmanuel and Dalissier, Arnaud and Rihani, Rawad and Alsaedi, Hawazen and Wynn, Robert F. and Dalle, Jean-Hugues and Peffault de Latour, Regis and Sedlacek, Petr and Balduzzi, Adriana and Schroeder, Thomas and Bodova, Ivana and Gonzalez Vicent, Marta and Gruhn, Bernd and Hamladji, Rose-Marie and Krivan, Gergely and Patrick, Katharine and Sobkowiak-Sobierajska, Agnieszka and Stepensky, Polina and Unal, Ali and Amrolia, Persis and Perez Martinez, Antonio and Rialland, Fanny and Aljurf, Mahmoud and Isgro, Antonella and Toren, Amos and Bierings, Marc and Corbacioglu, Selim and Kalwak, Krzysztof (2024) Outcomes of allogeneic haematopoietic cell transplantation for myelofibrosis in children and adolescents: the retrospective study of the EBMT Paediatric Diseases WP. BONE MARROW TRANSPLANTATION, 59 (8). pp. 1057-1069. ISSN 0268-3369, 1476-5365

Wang, Kevin and Coutifaris, Paulina and Brocks, David and Wang, Guanning and Azar, Tarek and Solis, Sabrina and Nandi, Ajeya and Anderson, Shaneaka and Han, Nicholas and Manne, Sasikanth and Kiner, Evgeny and Sachar, Chirag and Lucas, Minke and George, Sangeeth and Yan, Patrick K. and Kier, Melanie W. and Laughlin, Amy I. and Kothari, Shawn and Giles, Josephine and Mathew, Divij and Ghinnagow, Reem and Alanio, Cecile and Flowers, Ahron and Xu, Wei and Tenney, Daniel J. and Xu, Xiaowei and Amaravadi, Ravi K. and Karakousis, Giorgos C. and Schuchter, Lynn M. and Buggert, Marcus and Oldridge, Derek and Minn, Andy J. and Blank, Christian and Weber, Jeffrey S. and Mitchell, Tara C. and Farwell, Michael D. and Herati, Ramin S. and Huang, Alexander C. (2024) Combination anti-PD-1 and anti-CTLA-4 therapy generates waves of clonal responses that include progenitor-exhausted CD8<SUP>+</SUP> T cells. CANCER CELL, 42 (9). ISSN 1535-6108, 1878-3686

Weiler-Wichtl, Liesa J. and Fohn-Erhold, Verena and Rosenmayr, Verena and Hansl, Rita and Hopfgartner, Maximilian and Pal-Handl, Katharina and Wasinger-Brandweiner, Verena and Herzog, Kristina and Neumann, Kirsten and Schellenberg, Tobias and Schonenberger-Loppacher, Dorothee and Faist-Schweika, Christiane and Schonthaler, Barbara and Budich, Mihaela and Stember, Nicole and Wiegele, Karin and Reddig, Maike and Paduch, Anne and Lein-Koehler, Iris and Goergen, Sonja and Wienands, Heike and Gauf, Hiltrud and Hoffmann, Rahel and Kollmann, Alina and Just, Ulrike and Salzmann, Nicole and Neunsinger, Petra and Gerhardt, Marina and Essl, Stefanie and Borbely, Janina and Koepper, Manuel and Rinner, Sarah and Schubert, Lisa and Leiss, Ulrike (2024) Benefits of applying standardized frameworks to implement psychosocial tools such as the 'My Logbook'. SUPPORTIVE CARE IN CANCER, 32 (12): 789. ISSN 0941-4355, 1433-7339

Wiestler, Benedikt and Bison, Brigitte and Behrens, Lars and Tuechert, Stefanie and Metz, Marie and Griessmair, Michael and Jakob, Marcus and Schlegel, Paul-Gerhardt and Binder, Vera and von Luettichau, Irene and Metzler, Markus and Johann, Pascal and Hau, Peter and Fruehwald, Michael (2024) Human-Level Differentiation of Medulloblastoma from Pilocytic Astrocytoma: A Real-World Multicenter Pilot Study. CANCERS, 16 (8): 1474. ISSN 2072-6694