Safety and Efficacy Results with a Single Dose of Autologous CRISPR-Cas9-Modified CD34(+) Hematopoietic Stem and Progenitor Cells (HSPCs) in Transfusion-Dependent beta-Thalassemia (TDT) and Sickle Cell Disease (SCD)

Ho, T. W. and Frangoul, H. and Bobruff, Y. and Cappellini, M. D. and Corbacioglu, Selim and Fernandez, C. M. and de la Fuente, J. and Grupp, S. and Handgretinger, R. and Imren, S. and Kattamis, A. and Lekstrom-Himes, J. and Locatelli, F. and Lu, Y. and Mapara, M. and Mulcahey, S. and de Montalembert, M. and Rondelli, D. and Shanbhag, N. and Sheth, S. and Soni, S. and Steinberg, M. H. and Weinstein, M. and Wu, J. and Wall, D. (2021) Safety and Efficacy Results with a Single Dose of Autologous CRISPR-Cas9-Modified CD34(+) Hematopoietic Stem and Progenitor Cells (HSPCs) in Transfusion-Dependent beta-Thalassemia (TDT) and Sickle Cell Disease (SCD). In: 24th Annual Meeting of the American Society of Gene & Cell Therapy, May 11 - 14, 2021, Virtual.

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Item Type:	Conference or Workshop Item (UNSPECIFIED)
Subjects:	600 Technology > 610 Medical sciences Medicine
Divisions:	Medicine > Abteilung für Pädiatrische Hämatologie, Onkologie und Stammzelltransplantation
Depositing User:	Petra Gürster
Date Deposited:	18 Jan 2023 07:57
Last Modified:	18 Jan 2023 07:57
URI:	https://pred.uni-regensburg.de/id/eprint/47663

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