Early safety and efficacy results with a single dose of autologous CRISPR-Cas9-modified CD34+hematopoietic stem and progenitor cells in transfusion-dependent beta-thalassemia and sickle cell disease

de la Fuente, Josu and Frangoul, Haydar and Bobruff, Yael and Cappellini, Maria Domenica and Corbacioglu, Selim and Fernandez, Christine Marie and Grupp, Stephan and Handgretinger, Rupert and Ho, Tony W. and Imren, Suzan and Kattamis, Antonis and Lekstrom-Himes, Julie and Locatelli, Franco and Lu, Yimeng and Mapara, Markus and Mulcahey, Sarah and de Montalembert, Mariane and Rondelli, Damiano and Shanbhag, Niraj and Sheth, Sujit and Soni, Sandeep and Steinberg, Martin H. and Weinstein, Michael and Wu, John and Wall, Donna (2021) Early safety and efficacy results with a single dose of autologous CRISPR-Cas9-modified CD34+hematopoietic stem and progenitor cells in transfusion-dependent beta-thalassemia and sickle cell disease. In: 61st Annual Scientific Meeting of the British Society for Haematology, 25 – 28 April 2021, Virtual.

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Item Type: Conference or Workshop Item (Speech)
Subjects: 600 Technology > 610 Medical sciences Medicine
Divisions: Medicine > Abteilung für Pädiatrische Hämatologie, Onkologie und Stammzelltransplantation
Depositing User: Petra Gürster
Date Deposited: 18 Jan 2023 09:59
Last Modified: 18 Jan 2023 09:59
URI: https://pred.uni-regensburg.de/id/eprint/47944

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